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Clemidsogene Lanparvovec
clemidsogene lanparvovec
Adult Dosing .
Dosage forms: INJ
Investigational New Drug (IND)
- [FDA approval denied, February 2026]
mucopolysaccharidosis II
- [FDA approval denied]
- Info: recombinant adeno-associated viral vector delivers functional copy of iduronate-2-sulfatase gene to central nervous system
Peds Dosing .
- Dosage forms: INJ
Investigational New Drug (IND)
- [FDA approval denied, February 2026]
mucopolysaccharidosis II
- [FDA approval denied]
- Info: recombinant adeno-associated viral vector delivers functional copy of iduronate-2-sulfatase gene to central nervous system